ROCKET PHARMACEUTICALS, INC.
Business
ROCKET PHARMACEUTICALS, INC. is a fully integrated, late‑stage biotechnology company developing first‑in‑class in vivo and ex vivo gene therapies that target rare, often pediatric, monogenic diseases. Its main products are AAV‑based in vivo programs (e.g., Danon disease, PKP2‑ACM, BAG3‑DCM) and lentiviral ex vivo programs (e.g., LAD‑I, Fanconi anemia, pyruvate kinase deficiency). The company organizes its pipeline into cardiovascular and hematology programmatic segments and maintains cGMP manufacturing and licensing arrangements to support development and commercialization. It conducts clinical trials and seeks regulatory approvals across the U.S., European Union and other global markets with worldwide commercialization rights under license agreements.
Summary from filing dated 2025-02-27
Financials
Consolidated Statement of Income
| Concept | Trend | FY 2025 2025-12-31 | FY 2024 2024-12-31 | FY 2023 2023-12-31 | FY 2022 2022-12-31 | FY 2021 2021-12-31 |
|---|---|---|---|---|---|---|
| Revenue | 0 | 0 | 0 | 0 | 0 | |
| Research and development | 142 | 171 | 186 | 166 | 125 | |
| General and administrative | 87 | 102 | 73 | 59 | 42 | |
| Restructuring | 3 | 0 | — | — | — | |
| Total operating expenses | 232 | 273 | 260 | 224 | 167 | |
| Loss from operations | −232 | −273 | −260 | −224 | −167 | |
| Interest expense | −2 | −2 | −2 | −2 | −3 | |
| Interest and other income, net | 3 | 8 | 5 | 4 | 3 | |
| Accretion of discount on investments, net | 7 | 8 | 11 | −47,000 | −3 | |
| Net loss | −223 | −259 | −246 | −222 | −169 | |
| Net loss per share - basic (in dollars per share) | −2.01 | −2.73 | −2.92 | −3.26 | −2.67 | |
| Net loss per share - diluted (in dollars per share) | −2.01 | −2.73 | −2.92 | −3.26 | −2.67 | |
| Weighted-average common shares outstanding - basic (in shares) | 111 | 95 | 84 | 68 | 63 | |
| Weighted-average common shares outstanding - diluted (in shares) | 111 | 95 | 84 | 68 | 63 |
Consolidated Balance Sheet
| Concept | Trend | FY 2025 2025-12-31 | FY 2024 2024-12-31 | FY 2023 2023-12-31 | FY 2023 2023-03-31 | FY 2022 2022-12-31 |
|---|---|---|---|---|---|---|
| Cash and cash equivalents | 78 | 164 | 56 | — | 141 | |
| Investments | 111 | 209 | 317 | — | 216 | |
| Prepaid expenses and other current assets | 4 | 6 | 5 | — | 8 | |
| Total current assets | 193 | 378 | 378 | — | 364 | |
| Property and equipment, net | 28 | 37 | 39 | — | 29 | |
| Goodwill | 39 | 39 | 39 | — | 39 | |
| Intangible assets | 25 | 25 | 25 | — | 26 | |
| Restricted cash | 1 | 1 | 1 | — | 1 | |
| Deposits | 482,000 | 529,000 | 533,000 | — | 608,000 | |
| Operating lease right-of-use assets, net | 3 | 4 | 4 | 200,000 | 2 | |
| Finance lease right-of-use asset, net | 40 | 42 | 45 | — | 47 | |
| Total assets | 330 | 528 | 566 | — | 552 | |
| Accounts payable and accrued expenses | 27 | 38 | 46 | — | 37 | |
| Operating lease liabilities, current | 1 | 1 | 925,000 | — | 773,000 | |
| Finance lease liability, current | 2 | 2 | 2 | — | 2 | |
| Total current liabilities | 30 | 41 | 49 | — | 39 | |
| Operating lease liabilities, non-current | 3 | 3 | 3 | 200,000 | 1 | |
| Finance lease liability, non-current | 19 | 19 | 19 | — | 19 | |
| Other liabilities | 1 | 1 | 3 | — | 3 | |
| Total liabilities | 53 | 64 | 74 | — | 62 | |
| Commitments and contingencies (Note 14) | — | — | — | — | — | |
| Common stock, $0.01 par value, 180,000,000 shares authorized; 108,319,783 and 106,453,818 shares issued and outstanding as of December 31, 2025, and December 31, 2024, respectively | 1 | 1 | 903,000 | — | 791,000 | |
| Additional paid-in capital | 1,717 | 1,680 | 1,451 | — | 1,203 | |
| Accumulated other comprehensive (loss) income | −31,000 | 66,000 | 319,000 | — | −357,000 | |
| Accumulated deficit | −1,440 | −1,218 | −959 | — | −714 | |
| Total stockholders' equity | 277 | 463 | 493 | — | 490 | |
| Total liabilities and stockholders' equity | 330 | 528 | 566 | — | 552 |
Consolidated Statement of Cash Flows
| Concept | Trend | FY 2025 2025-12-31 | FY 2024 2024-12-31 | FY 2023 2023-12-31 | FY 2022 2022-12-31 | FY 2021 2021-12-31 |
|---|---|---|---|---|---|---|
| Depreciation and amortization of property and equipment | 9 | 7 | 5 | 4 | 3 | |
| Amortization of finance lease right of use asset | 2 | 2 | 2 | 2 | 2 | |
| Impairment of operating lease right-of-use asset | 262,000 | 0 | — | — | — | |
| Stock-based compensation | 37 | 44 | 39 | 31 | 29 | |
| Accretion of discount on investments, net | −7 | −8 | −10 | 134,000 | 3 | |
| Change in fair value of warrant liabilities | 0 | −2 | −364,000 | — | — | |
| Prepaid expenses and other assets | 2 | −661,000 | 3 | −4 | 1 | |
| Accounts payable and accrued expenses | −10 | 6 | 10 | 10 | −5 | |
| Operating lease liabilities and right of use assets, net | 45,000 | 89,000 | 137,000 | −120,000 | −11,000 | |
| Finance lease liability | 35,000 | 95,000 | 139,000 | 172,000 | 201,000 | |
| Other liabilities | −81,000 | 81,000 | 705,000 | −57,000 | −56,000 | |
| Net cash used in operating activities | −190 | −210 | −195 | −178 | −121 | |
| Purchases of investments | −277 | −246 | −391 | −376 | −246 | |
| Proceeds from maturities of investments | 381 | 383 | 309 | 273 | 272 | |
| Purchases of property and equipment | −440,000 | −6 | −16 | −8 | −8 | |
| Net cash provided by investing activities | 104 | 132 | −98 | −69 | 19 | |
| Issuance of common stock pursuant to exercise of stock options | 0 | 3 | 2 | 631,000 | 11 | |
| Return of related party short-swing profits | 215,000 | 0 | — | — | — | |
| Repurchase of restricted stock units to satisfy tax withholding | −67,000 | 0 | — | — | — | |
| Net cash provided by financing activities | 148,000 | 186 | 208 | 155 | 38 | |
| Net change in cash, cash equivalents and restricted cash | −86 | 108 | −85 | −92 | −65 | |
| Accrued purchases of property and equipment, ending balance | 0 | 185,000 | 1 | 2 | 728,000 | |
| Receivables from sale of property and equipment, ending balance | 0 | 135,000 | 0 | 0 | — | |
| Operating lease liabilities | 0 | 1 | 3 | 0 | 0 | |
| Operating lease right of use assets | 0 | 1 | 3 | 0 | — | |
| Net unrealized loss on investments | −100,000 | −300,000 | 700,000 | −200,000 | −100,000 |