18. Segment Information

Segment reporting is prepared on the same basis that the Company's chief executive officer, who is the Company's chief operating decision maker (the “CODM”), utilizes to manage the business and makes decisions on how to allocate resources and assess performance of the business. The Company and the CODM view the Company's operations as a single operating segment. The Company's singular focus is on developing small molecules to improve the lives of patients with genetically defined rare diseases in areas of high unmet medical need.

The Company and the CODM primarily utilize the segment's consolidated net loss, disaggregated between (a) research and development and (b) general and administrative, as the key indicator to assess the segment's performance and for allocating resources.

The Company's reportable segment revenue, operating expenses, and net loss for the years ended December 31, 2025 and December 31, 2024 are as follows:

 

 

 

Year Ended
December 31,

 

 

 

2025

 

 

2024

 

Collaboration Revenue

 

 

 

 

 

80,000

 

Operating expenses:

 

 

 

 

 

 

Research and development

 

 

 

 

 

 

Pociredir external expenses

 

 

19,994

 

 

 

8,577

 

Losmapimod external expenses

 

 

941

 

 

 

20,801

 

Employee compensation expenses (excluding stock-based compensation expenses)

 

 

12,659

 

 

 

15,347

 

Stock-based compensation expenses

 

 

3,448

 

 

 

4,653

 

Pre-development candidate expenses and unallocated expenses

 

 

19,061

 

 

 

14,008

 

General and administrative

 

 

28,666

 

 

 

36,448

 

Restructuring expenses

 

 

 

 

 

2,063

 

Total operating expenses

 

 

84,769

 

 

 

101,897

 

Loss from operations

 

 

(84,769

)

 

 

(21,897

)

Other income, net

 

 

9,889

 

 

 

12,172

 

Net loss

 

$

(74,880

)

 

$

(9,725

)

Historical Timeline

Fiscal YearFiled
2025Feb 24, 2026Showing above
2024Feb 25, 2025

About Segments Disclosures

Segment disclosures break a company into its reportable operating units, revealing revenue, profit, and asset allocation that consolidated financial statements obscure. Under ASC 280, segments must match how the chief operating decision maker views the business, providing a window into internal management structure and resource allocation priorities.

Key signals: compare segment margins to identify which units drive profitability and which destroy value. Watch for changes in the number of reportable segments — segment aggregation or disaggregation often coincides with strategic shifts or attempts to obscure declining performance. Intersegment elimination patterns reveal internal pricing practices. The reconciliation between segment totals and consolidated figures exposes corporate overhead allocation and unallocated items. Geographic revenue concentration highlights regulatory and currency exposure. Compare segment-level capital expenditure against segment revenue to assess where management is investing for future growth versus harvesting existing assets.